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American Academy of Pediatrics
Article

What the Orphan Drug Act Has Done Lately for Children With Rare Diseases: A 10-Year Analysis

Chandana Thorat, Kui Xu, Scott N. Freeman, Renan A. Bonnel, Francesca Joseph, M. Ian Phillips and Menfo A. Imoisili
Pediatrics March 2012, 129 (3) 516-521; DOI: https://doi.org/10.1542/peds.2011-1798
Chandana Thorat
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Kui Xu
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Scott N. Freeman
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Renan A. Bonnel
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Francesca Joseph
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M. Ian Phillips
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Menfo A. Imoisili
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Article Information

vol. 129 no. 3 516-521
DOI 
https://doi.org/10.1542/peds.2011-1798
PubMed 
22371464

Published By 
American Academy of Pediatrics
Print ISSN 
0031-4005
Online ISSN 
1098-4275
History 
  • Accepted October 27, 2011
  • Published online March 1, 2012.

Article Versions

  • previous version (February 27, 2012 - 00:08).
  • You are viewing the most recent version of this article.
Copyright & Usage 
Copyright © 2012 by the American Academy of Pediatrics

Author Information

  1. Chandana Thorat, BTecha,
  2. Kui Xu, MD, PhDb,
  3. Scott N. Freeman, PhDb,
  4. Renan A. Bonnel, PharmD, MPHc,
  5. Francesca Joseph, MDb,
  6. M. Ian Phillips, PhD, DSca, and
  7. Menfo A. Imoisili, MD, MPHb
  1. aKeck Graduate Institute of Applied Life Sciences, Center for Rare Disease Therapies, Claremont, California; and
  2. Offices of bOrphan Products Development and
  3. cPediatric Therapeutics, Office of the Commissioner, US Food and Drug Administration, Silver Spring, Maryland
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Pediatrics
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1 Mar 2012
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What the Orphan Drug Act Has Done Lately for Children With Rare Diseases: A 10-Year Analysis
Chandana Thorat, Kui Xu, Scott N. Freeman, Renan A. Bonnel, Francesca Joseph, M. Ian Phillips, Menfo A. Imoisili
Pediatrics Mar 2012, 129 (3) 516-521; DOI: 10.1542/peds.2011-1798

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What the Orphan Drug Act Has Done Lately for Children With Rare Diseases: A 10-Year Analysis
Chandana Thorat, Kui Xu, Scott N. Freeman, Renan A. Bonnel, Francesca Joseph, M. Ian Phillips, Menfo A. Imoisili
Pediatrics Mar 2012, 129 (3) 516-521; DOI: 10.1542/peds.2011-1798
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